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IQVIA™ Real-World Insights Bibliography

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Condition: Rare disease

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Total number of items in this bibliography: 13

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Physician awareness and understanding of hereditary angioedema: a web-based study in Japan
Author(s): Atsushi Fukunaga 1,2, Miwa Kishimoto 3*, Akinori Oh 3, Takeshi Akiyama 4, Ippei Kotera 3, Yoichi Inoue 3, Junichi Maehara 5 (rwesheorj 4)
Affiliations(s): 1) Division of Dermatology, Department of Internal Related, Kobe University Graduate School of Medicine, Hyogo, Japan 2) Division of Medicine for Function and Morphology of Sensory Organs, Department of Dermatology, Faculty of Medicine, Osaka Medical and Pharmaceutical University, Takatsuki, Japan 3) Japan Medical Office, Takeda Pharmaceutical Company Limited, Tokyo, Japan 4) Real World Evidence Solutions & HEOR, IQVIA Solutions Japan K.K., Tokyo, Japan 5) Department of Acute Care and General Medicine, Emergency and Critical Care Center, Saiseikai Kumamoto Hospital, Kumamoto, Japan
Publication(s): Journal of Cutaneous Immunology and Allergy.
Document Type(s): Article,
Countries: Japan,
Click here for the abstract
C: Y:	Rare disease, 2022	L: A:	English Survey research,


CO71 Investigating the Secondary Care System Burden of Glycogen Storage Disease Type IA (GSDIA) Using the HES Database
Author(s): E Kruger S Chavda RN Gupta V Valayannopoulos
Affiliations(s): Ultragenyx Pharmaceutical Inc., Novato, CA, USA IQVIA, London, UK Ultragenyx Pharmaceutical Inc., Cambridge, MA, USA
Publication(s): Kruger, E et al. Value in Health, Volume 25, Issue 7, S317
Document Type(s): Abstract, Article,
Countries: England,
Click here for the abstract
C: Y:	Metabolic Disorders , Rare disease, Rare Diseases, 2022	L: A:	English Burden of illness, clinical setting: Secondary care, Quality of life,


Leveraging unstructured data to identify hereditary angioedema patients in electronic medical records
Author(s): Emily S Brouwer 1 , Emily W Bratton 2 , Aimee M Near 2 , Lynn Sanders 1 , Christina D Mack 2
Affiliations(s): 1 Takeda Pharmaceutical Company Limited, 300 Shire Way, Lexington, MA, USA. 2 IQVIA, Durham, NC, USA.
Publication(s): Allergy Asthma Clin Immunol . 2021 Apr 20;17(1):41. doi: 10.1186/s13223-021-00541-6.
Document Type(s): Article,
Countries: USA,
Click here for the abstract
C: Y:	Rare disease, 2021	L: A:	English Clinical setting: Primary care, clinical setting: Secondary care, Epidemiological study, Observational study, Retrospective database analysis,


A budget impact analysis of anti-inhibitor coagulant complex use in pediatric hemophilia A patients with inhibitors across kingdom of Saudi Arabia
Author(s): Al Jedai A1, AL-Mudaiheem H1, Al daamah S2, Al kasim F3, Wasri A4, Shaheen N5, Dawood E6, El-Hamaidi I7, Mohamed O8
Affiliations(s): 1Ministry of Health, Riyadh, NJ, USA, 2Ministry of Health, Damam, Saudi Arabia, 3Ministry of Health, Riyadh, Saudi Arabia, 4Ministry of National Guards, Jeddah, Saudi Arabia, 5King Faisal Specialized Hospitals, Damam, Saudi Arabia, 6Ministry of Health, Mekkah, Saudi Arabia, 7Ministry of National Guards, Riyadh, Saudi Arabia, 8IQVIA, Dubai, DU, United Arab Emirates
Publication(s): 2019-11, ISPOR Europe 2019, Copenhagen, Denmark
Document Type(s): Poster,
Countries: Saudi Arabia,
Click here for the abstract
C: Y:	Hematology, Rare disease, 2019	L: A:	English Budget impact,


Cost-utility analysis of life-long prophylaxis with recombinant factor VIIIFc vs recombinant factor VIII for the management of severe hemophilia A in Sweden.
Author(s): Henry N1, JovanoviÄ‡ J1, Schlueter M1, Kritikou P2, Wilson K2, MyrÃ©n KJ2.
Affiliations(s): Henry N1, JovanoviÄ‡ J1, Schlueter M1, Kritikou P2, Wilson K2, MyrÃ©n KJ2. 1 IQVIA , London , UK. 2 Swedish Orphan Biovitrum AB , Stockholm , Sweden.
Publication(s):
Document Type(s): Article,
Countries: Nordic, UK,
C: Y:	Hematology, Rare disease, 2018	L: A:	English Retrospective database analysis,


Angiotensin II receptor blockers and intestinal malabsorption: an observational cohort study in Germany and Italy
Author(s): Malfertheiner P1, Heiman F2, Ripellino C3, Cataldo N2
Affiliations(s): 1 Otto-von-Guericke Universität, Klinik für Gastroenterologie, Hepatologie und Infektiologie 2 QuintilesIMS, Milan, Italy 3 HEOR Consultant, Freelance, Milan, Italy
Publication(s): ISPOR 20th Annual European Congress, 4-8 November 2017, Glasgow, Scotland
Document Type(s): Poster,
Countries: Germany, Italy,
C: Y:	Drug safety, Gastrointestinal disorders, Rare disease, 2017	L: A:	English Database Study, Epidemiological study, Longitudinal study, Observational study, Population Based Study, Real World Data, Real World Evidence, Retrospective cohort analysis, Retrospective database analysis,


Real-world Assessment of Renal Involvement in Tuberous Sclerosis Complex (TSC) Patients in the United Kingdom (UK): A Retrospective Cohort Study in the Clinical Practice Research Datalink (CPRD)
Author(s): Kingswood, Chris1, Nasuti, Paola2, Demuth, Dirk2, Patel, Keyur2, Myland, Melissa2, Erhard, Clement3, Gray, Elizabeth4, Pinnegar, Alun4, Magestro, Matthew5
Affiliations(s): The Royal Sussex County Hospital, Brighton, England 2 IMS Health, London, UK 3 CE Analytics, Cambridge, UK 4 Novartis Pharmaceuticals UK Ltd, Frimley, UK 5 Novartis Pharmaceuticals Corporation, East Hanover NJ, USA
Publication(s): International TSC Research Conference (Windsor, 11th Sept 2015).
Document Type(s): Poster,
Countries: England,
C: Y:	Oncology, Pediatrics, Rare disease, 2015	L: A:	English Retrospective cohort analysis,


Association of sweat chloride concentration at time of diagnosis and CFTR genotype with mortality and cystic fibrosis phenotype
Author(s): McKone EF, Goss C, Velentgas P, Swenson A
Affiliations(s):
Publication(s): Journal of Cystic Fibrosis. JCF1155. Feb 2015. 10.1016(j.jcf.2015) 01.005
Document Type(s): Article,
Countries:
C: Y:	Rare disease, 2015	L: A:	English RWLPR (Real-World Late Phase Research-quintiles,


Fifth interim analysis of the Kuvan® Adult Maternal Paediatric European Registry (KAMPER): Insights into management/practice in patients with PKU.
Author(s): Lagler FB, Muntau AC, Feillet F, Rogoff D, Moreau-Stucker F, Alm J, Burlina A, Trefz FK.
Affiliations(s): Quintiles Real-World and Late Phase Research
Publication(s): Society for the Study of Inborn Errors of Metabolism (SSIEM) Annual Congress, 1â€“4 September 2015, Lyon, France, Abstract No. P-160
Document Type(s): Abstract,
Countries:
C: Y:	Patient Registries & Real-World Study Methods, Rare disease, 2015	L: A:	English RWLPR (Real-World Late Phase Research-quintiles,


Impact of Acute Bleeding on Daily Activities of Patients with Congenital Hemophilia with Inhibitors and Their Caregivers and Families: Observations from the Dosing Observational Study in Hemophilia (DOSE). Science Direct
Author(s): Recht N, Neufeld EJ, Sharma VR, Solem CT, Pickard S, Gut RZ, MD, Cooper DL
Affiliations(s):
Publication(s):
Document Type(s): Article,
Countries:
C: Y:	Rare disease, 2014	L: A:	English RWLPR (Real-World Late Phase Research-quintiles,


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